CRISPR-Cas9: A method for establishing rat models of drug metabolism and pharmacokinetics - ScienceDirect
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Clinical trials and promising preclinical applications of CRISPR/Cas gene editing - ScienceDirect
The Pharmacokinetics and Pharmacodynamics of A Novel Recombinant Activated Human Factor VII, GEN-0828, in Hemophilia B Mice - Journal of Pharmaceutical Sciences
Morquio Syndrome (Mucopolysaccharidosis Type IV) Treatment & Management: Approach Considerations, Medical Care, Surgical Care
Efficient manufacturing and engraftment of CCR5 gene-edited HSPCs following busulfan conditioning in nonhuman primates: Molecular Therapy - Methods & Clinical Development
The Pharmacokinetics and Pharmacodynamics of A Novel Recombinant Activated Human Factor VII, GEN-0828, in Hemophilia B Mice - Journal of Pharmaceutical Sciences
CRISPR-Cas9: A method for establishing rat models of drug metabolism and pharmacokinetics - ScienceDirect
Functional restoration of a CFTR splicing mutation through RNA delivery of CRISPR adenine base editor: Molecular Therapy
PDF) Human and Mouse Artificial Chromosome Technologies for Studies of Pharmacokinetics and Toxicokinetics
Frontiers CRISPR/Cas9: implication for modeling and therapy of amyotrophic lateral sclerosis
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