CRISPR-Cas9 correction of OPA1 c.1334G>A: p.R445H restores mitochondrial homeostasis in dominant optic atrophy patient-derived iPSCs - ScienceDirect

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CRISPR-Cas9 correction of OPA1 c.1334G>A: p.R445H restores mitochondrial  homeostasis in dominant optic atrophy patient-derived iPSCs - ScienceDirect
Cold shock' increases the frequency of homology directed repair gene editing in induced pluripotent stem cells
CRISPR-Cas9 correction of OPA1 c.1334G>A: p.R445H restores mitochondrial  homeostasis in dominant optic atrophy patient-derived iPSCs - ScienceDirect
CRISPR/Cas9-based targeting of fluorescent reporters to human iPSCs to isolate atrial and ventricular-specific cardiomyocytes
CRISPR-Cas9 correction of OPA1 c.1334G>A: p.R445H restores mitochondrial  homeostasis in dominant optic atrophy patient-derived iPSCs - ScienceDirect
Comprehensive transcriptome-wide analysis of spliceopathy correction of myotonic dystrophy using CRISPR-Cas9 in iPSCs-derived cardiomyocytes: Molecular Therapy
CRISPR-Cas9 correction of OPA1 c.1334G>A: p.R445H restores mitochondrial  homeostasis in dominant optic atrophy patient-derived iPSCs - ScienceDirect
PDF) CRISPR/Cas9 correction of OPA1 c.1334G>A: p.R445H restores mitochondrial homeostasis in Dominant Optic Atrophy patient-derived iPSCs
CRISPR-Cas9 correction of OPA1 c.1334G>A: p.R445H restores mitochondrial  homeostasis in dominant optic atrophy patient-derived iPSCs - ScienceDirect
CRISPR genome surgery in a novel humanized model for autosomal dominant retinitis pigmentosa: Molecular Therapy
CRISPR-Cas9 correction of OPA1 c.1334G>A: p.R445H restores mitochondrial  homeostasis in dominant optic atrophy patient-derived iPSCs - ScienceDirect
PDF) CRISPR/Cas9 correction of OPA1 c.1334G>A: p.R445H restores mitochondrial homeostasis in Dominant Optic Atrophy patient-derived iPSCs
CRISPR-Cas9 correction of OPA1 c.1334G>A: p.R445H restores mitochondrial  homeostasis in dominant optic atrophy patient-derived iPSCs - ScienceDirect
Targeted Repair of p47-CGD in iPSCs by CRISPR/Cas9: Functional Correction without Cleavage in the Highly Homologous Pseudogenes - ScienceDirect
CRISPR-Cas9 correction of OPA1 c.1334G>A: p.R445H restores mitochondrial  homeostasis in dominant optic atrophy patient-derived iPSCs - ScienceDirect
Urban particulate matter disturbs the equilibrium of mitochondrial dynamics and biogenesis in human vascular endothelial cells - ScienceDirect
CRISPR-Cas9 correction of OPA1 c.1334G>A: p.R445H restores mitochondrial  homeostasis in dominant optic atrophy patient-derived iPSCs - ScienceDirect
High-throughput phenotypic screen for genetic modifiers in patient-derived OPA1 mutant fibroblasts identifies PGS1 as a functional suppressor of mitochondrial fragmentation
CRISPR-Cas9 correction of OPA1 c.1334G>A: p.R445H restores mitochondrial  homeostasis in dominant optic atrophy patient-derived iPSCs - ScienceDirect
CRISPR/Cas9-based targeting of fluorescent reporters to human iPSCs to isolate atrial and ventricular-specific cardiomyocytes
CRISPR-Cas9 correction of OPA1 c.1334G>A: p.R445H restores mitochondrial  homeostasis in dominant optic atrophy patient-derived iPSCs - ScienceDirect
Nanoparticles-mediated CRISPR-Cas9 gene therapy in inherited retinal diseases: applications, challenges, and emerging opportunities, Journal of Nanobiotechnology
CRISPR-Cas9 correction of OPA1 c.1334G>A: p.R445H restores mitochondrial  homeostasis in dominant optic atrophy patient-derived iPSCs - ScienceDirect
PDF) CRISPR/Cas9 correction of OPA1 c.1334G>A: p.R445H restores mitochondrial homeostasis in Dominant Optic Atrophy patient-derived iPSCs
CRISPR-Cas9 correction of OPA1 c.1334G>A: p.R445H restores mitochondrial  homeostasis in dominant optic atrophy patient-derived iPSCs - ScienceDirect
Co-opting regulation bypass repair as a gene-correction strategy for monogenic diseases: Molecular Therapy
CRISPR-Cas9 correction of OPA1 c.1334G>A: p.R445H restores mitochondrial  homeostasis in dominant optic atrophy patient-derived iPSCs - ScienceDirect
PDF) CRISPR/Cas9 correction of OPA1 c.1334G>A: p.R445H restores mitochondrial homeostasis in Dominant Optic Atrophy patient-derived iPSCs
CRISPR-Cas9 correction of OPA1 c.1334G>A: p.R445H restores mitochondrial  homeostasis in dominant optic atrophy patient-derived iPSCs - ScienceDirect
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