Niemann–Pick type C disease: cellular pathology and
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The pathogenesis of Niemann–Pick type C disease: a role for autophagy?, Expert Reviews in Molecular Medicine
Niemann-Pick disease types A and B (NORD): Video
Niemann–Pick disease - Wikipedia
Hepatocellular carcinoma as a complication of Niemann‐Pick disease type C1 - Rodriguez‐Gil - 2021 - American Journal of Medical Genetics Part A - Wiley Online Library
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Imaging of neuroinflammation in adult Niemann-Pick type C disease
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PDF) The pathogenesis of Niemann-Pick type C disease: A role for autophagy?
Disruptive lysosomal-metabolic signaling and neurodevelopmental deficits that precede Purkinje cell loss in a mouse model of Niemann-Pick Type-C disease
Niemann Pick Disease
Niemann–Pick disease type C1 (NPC1) is associated with early-onset
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PDF] Niemann-Pick Type C Disease—Pathophysiology and Future Perspectives for Treatment
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